PUBLICATION

Zebrafish mafbb Mutants Display Osteoclast Over-Activation and Bone Deformity Resembling Osteolysis in MCTO Patients

Authors
Han, Y., Shao, W., Zhong, D., Ma, C., Wei, X., Ahmed, A., Yu, T., Jing, W., Jing, L.
ID
ZDB-PUB-210407-42
Date
2021
Source
Biomolecules   11(3): (Journal)
Registered Authors
Jing, Lili
Keywords
MAFB, Multicentric Carpotarsal Osteolysis (MCTO), macrophage and monocytes, osteoclasts, zebrafish
MeSH Terms
  • Animals
  • Humans
  • Maf Transcription Factors/genetics*
  • Mutation/genetics
  • Oncogene Proteins/genetics*
  • Osteoclasts/metabolism*
  • Osteogenesis/physiology
  • Osteolysis/metabolism
  • Zebrafish
  • Zebrafish Proteins/genetics*
PubMed
33806930 Full text @ Biomolecules
Abstract
Multicentric carpotarsal osteolysis (MCTO) is a rare skeletal dysplasia with osteolysis at the carpal and tarsal bones. Heterozygous missense mutations in the transcription factor MAFB are found in patients with MCTO. MAFB is reported to negatively regulate osteoclastogenesis in vitro. However, the in vivo function of MAFB and its relation to MCTO remains unknown. In this study, we generated zebrafish MAFB homolog mafbb mutant utilizing CRISPR/Cas9 technology. Mafbb deficient zebrafish demonstrated enhanced osteoclast cell differentiation and abnormal cartilage and bone development resembling MCTO patients. It is known that osteoclasts are hematopoietic cells derived from macrophages. Loss of mafbb caused selective expansion of definitive macrophages and myeloid cells, supporting that mafbb restricts myeloid differentiation in vivo. We also demonstrate that MAFB MCTO mutations failed to rescue the defective osteoclastogenesis in mafbb-/- embryos, but did not affect osteoclast cells in wild type embryos. The mechanism of MCTO mutations is likely haploinsufficiency. Zebrafish mafbb mutant provides a useful model to study the function of MAFB in osteoclastogenesis and the related MCTO disease.
Genes / Markers
Figures
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Expression
Phenotype
Mutations / Transgenics
Human Disease / Model
Sequence Targeting Reagents
Fish
Antibodies
Orthology
Engineered Foreign Genes
Mapping